Transcutaneous photodynamic treatment of targeted cells

A - Human Necessities – 61 – K

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A61K 41/00 (2006.01)

Patent

CA 2356776

The present invention is drawn to methods and compounds for photodynamic therapy (PDT) of a target tissue or compositions in a mammalian subject, using a light source that preferably transmits light to a treatment site transcutaneously. The method provides for administering to the subject a therapeutically effective amount of a targeted substance, which is either a targeted photosensitizing agent, or a photosensitizing agent delivery system, or a targeted prodrug. This targeted substance preferably selectively binds to the target tissue. Light at a wavelength or waveband corresponding to that which is absorbed by the targeted substance is then administered. The light intensity is relatively low, but a high total fluence is employed to ensure the activation of the targeted photosensitizing agent or targeted prodrug product. Transcutaneous PDT is useful in the treatment of specifically selected target tissues, such as vascular endothelial tissue, the abnormal vascular walls of tumors, solid tumors of the head and neck, tumors of the gastrointestinal tract, tumors of the liver, tumors of the breast, tumors of the prostate, tumors of the lung, nonsolid tumors, malignant cells of the hermatopoietic and lymphoid tissue and other lesions in the vascular system or bone marrow, and tissue or cells related to autoimmune and inflammatory disease.

La présente invention concerne des méthodes et des composés destinés au traitement photodynamique de tissus ou de compositions cible chez un mammifère, lequel traitement utilise une source lumineuse émettant, de préférence, la lumière au niveau d'un site de traitement de façon transcutanée. La méthode consiste à administrer à un sujet une dose thérapeutiquement efficace d'une substance cible, c'est-à-dire soit un agent photosensibilisant cible, soit un système d'apport d'un agent photosensibilisant, soit un promédicament cible. De préférence, cette substance se lie sélectivement aux tissus cibles. On administre ensuite la lumière à une longueur d'onde ou une gamme d'onde correspondant à celle qui est absorbée par la substance cible. L'intensité de la lumière est relativement faible, mais on utilise une fluence totale élevée pour garantir l'activation de l'agent photosensibilisant cible ou du promédicament cible. La thérapie photodynamique transcutanée est utile pour traiter des tissus cible spécifiquement sélectionnés, tels que l'endothélium vasculaire, les parois vasculaires anormales des tumeurs, les tumeurs solides de la tête et du cou, les tumeurs du tractus gastro-intestinal, les tumeurs du foie, les tumeurs du sein, les tumeurs de la prostate, les tumeurs des poumons, les tumeurs non solides, les cellules malignes des tissus hématopoïétiques et lymphoïdes et autres lésions du système vasculaires ou de la moelle osseuse, ainsi que les tissus ou les cellules associés aux maladies autoimmunes et inflammatoires.

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