C - Chemistry – Metallurgy – 12 – N
Patent
C - Chemistry, Metallurgy
12
N
C12N 15/86 (2006.01) C07K 14/015 (2006.01) C12N 7/01 (2006.01) C12N 15/864 (2006.01) C12N 15/869 (2006.01) G01N 33/50 (2006.01)
Patent
CA 2306252
Preparations of infectious viral particles include viral particles which can act as helper virus for adeno-associated virus (AAV), and include particles comprising DNA (i) that includes at least one chosen nucleic acid sequence for delivery to target host cells, and further encoding proteins and replicating functions which together are sufficient, when said particles of said preparation infect first target host cells, for assembly and release, from said first target cells, of infectious recombinant AAV particles that comprise said chosen nucleic acid sequence whereby said infectious recombinant AAV particles are able in turn to infect second target host cells, and cause expression of said DNA (i) in said infected second target host cells.
L'invention concerne des préparations de particules virales infectieuses. Ces particules sont des particules virales qui peuvent agir comme virus assistants pour les virus associés aux adénovirus (AAV) et des particules qui renferment de l'ADN (i) contenant au moins une séquence d'acide nucléique choisie pour être introduite dans des cellules hôtes cibles et codant pour des protéines et des fonctions de réplication. Ces protéines et ces fonctions sont suffisantes, quand lesdites particules de ladite préparation infectent des premières cellules hôtes cibles, pour induire l'assemblage et la libération, à partir desdites premières cellules cibles, de particules d'AAV recombinantes contenant ladite séquence d'acide nucléique choisie. Ces particules d'AAV recombinantes sont capables à leur tour d'infecter des secondes cellules hôtes cibles et d'induire l'expression dudit ADN (i) dans lesdites secondes cellules hôtes cibles infectées.
Bereskin & Parr
Cantab Pharmaceuticals Research Limited
Xenova Research Limited
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