C - Chemistry – Metallurgy – 12 – N
Patent
C - Chemistry, Metallurgy
12
N
C12N 5/22 (2006.01) C12N 15/10 (2006.01) C12N 15/85 (2006.01) C12N 5/08 (2006.01)
Patent
CA 2409713
The present invention provides human neural crest stem cells which are pluripotent, self-renewing, and can be maintained as a stable cell line via retrovirus- mediated vmyc gene transfer. These human neural crest stem cells and their daughter progeny cells are uncommitted and undifferentiated cells which can subsequently be induced to a range of alternative recognized types of differentiated and functional cells including neurons, Schwann cells, adrenal chromaffin cells, and skeletal muscle cells. These human neural crest stem cells and their progeny cells are suitable for implantation in-vivo for cell therapy treatment of human neurological disorders and diseases.
La présente invention concerne des cellules souches de crête neurale humaine qui sont multipotentes, qui s'autorenouvellent et qui peuvent être maintenues comme des cellules souches stables via un transfert génique <u>vmyc</u> réalisé par des rétrovirus. Ces cellules souches de crête neurale humaine et leurs cellules-filles de descendance sont des cellules de réserve et indifférenciées qui peuvent ensuite être induites à une portée de types reconnus alternatifs de cellules différenciées et fonctionnelles, y compris des neurones, des cellules Schwann, des cellules des surrénales de tissu chromaffine, et des cellules musculaires du squelette. Ces cellules souches de crête neurale humaine et leurs cellules-filles de descendance sont appropriées pour une implantation in vivo lors d'un traitement thérapeutique cellulaire de maladies et de troubles neurologiques humains.
Kim Seung U.
Snyder Evan Y.
Wolfe John H.
Smart & Biggar
The Children's Medical Center Corporation
Trustees Of The University Of Pennsylvania
University Of British Columbia
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