Replication-competent herpes simplex viruses

A - Human Necessities – 01 – N

Patent

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A01N 63/00 (2006.01) A61K 39/12 (2006.01) A61K 39/245 (2006.01) A61K 48/00 (2006.01) C12N 7/04 (2006.01) C12N 15/869 (2006.01) C12P 15/00 (2006.01) C12P 21/06 (2006.01) A61K 38/00 (2006.01)

Patent

CA 2284611

A promising approach for the therapeutic treatment of brain tumors utilizes replication-competent, neuroattenuated herpes simplex virus-1 (HSV-1) mutants. This approach requires mutation of HSV-1 to eliminate killing of normal, non- dividing cells of the brain (e.g., neurons). The present invention discloses methods for killing malignant brain tumor cells in vivo entails providing replication competent herpes simplex virus vectors to tumor cells. A replication competent herpes simplex virus vector, with defective expression of the gamma 34.5 gene and the uracil DNA glycosylase (UNG) gene, specifically destroys tumor cells, is hypersensitive to anti-viral agents, and is not neurovirulent.

L'invention porte sur une méthode d'avenir s'appliquant au traitement thérapeutique des tumeurs cérébrales et qui met en oeuvre des mutants du virus simplex de l'herpès 1 (HSV-1) neuroatténués et aptes à la réplication. Cette méthode nécessite la mutation du HSV-1 pour empêcher la destruction des cellules cérébrales normales, non en cours de division (telles que les neurones). Cette invention porte également sur des procédés visant à tuer les cellules tumorales cérébrales malignes in vivo et sur la production de vecteurs du virus simplex de l'herpès aptes à la réplication contre les cellules tumorales, ainsi que sur un vecteur du virus simplex de l'herpès apte à la réplication, incapable d'exprimer le gène gamma 34.5 et le gène uracile ADN glycosylase, et qui détruit spécifiquement les cellules tumorales, est hypersensible aux agents antiviraux, mais n'est pas neurovirulent.

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