C - Chemistry – Metallurgy – 12 – N
Patent
C - Chemistry, Metallurgy
12
N
C12N 15/11 (2006.01) A61K 31/713 (2006.01)
Patent
CA 2688514
The present invention is directed to RNA interference (RNAi) molecules targeted against a nucleic acid sequence that encodes poly-glutamine repeat diseases, and methods of using these RNAi molecules.
La présente invention concerne des molécules d'interférence par l'ARN (ARNi) ciblées sur une séquence d'acide nucléique qui code pour des maladies de répétition de polyglutamine et des méthodes pour utiliser ces particules d'ARNi.
Boudreau Ryan L.
Davidson Beverly L.
Mas Monteys Alejandro
Bereskin & Parr Llp/s.e.n.c.r.l.,s.r.l.
University Of Iowa Research Foundation
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