Isolated homozygous stem cells differentiated cells derived...

C - Chemistry – Metallurgy – 12 – N

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C12N 5/00 (2006.01) C12N 5/0735 (2010.01) A61K 35/12 (2006.01)

Patent

CA 2430627

The present invention discloses and describes pluripotent homozygous stem (HS) cells, and methods and materials for making same. The present invention also provides methods for differentiation of HS cells into progenitor (multipotent) cells or other desired ! cells, groups of cells or tissues. Further, the applications of the HS cells disclosed herein, include (but are not limited to) the diagnosis and treatment of various diseases (for example, genetic diseases, neurodegenerative diseases, endocrine-related disorders and cancer), traumatic injuries, cosmetic or therapeutic transplantation, gene therapy and cell replacement therapy.

La présente invention concerne des cellules souches homozygotes pluripotentes, et des procédés et des matériaux permettant de les fabriquer. La présente invention concerne également des méthodes de différentiation de cellules souches homozygotes dans des cellules embryonnaires (multipotentes) ou autres cellules, groupes de cellules ou tissus souhaités. En outre, les applications des cellules souches homozygotes susmentionnées comprennent, entre autres, le diagnostic et le traitement de diverses maladies (par exemple, les maladies génétiques, les maladies neurodégénératives, les troubles endocriniens, et le cancer) et de lésions traumatiques, la transplantation à des fins cosmétiques ou thérapeutiques, la thérapie génique et la thérapie de remplacement cellulaire.

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