Transgenic plant-derived human blood coagulation factors

C - Chemistry – Metallurgy – 12 – N

Patent

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Details

C12N 15/12 (2006.01) A01H 5/00 (2006.01) A61K 38/36 (2006.01) C07K 14/745 (2006.01) C07K 14/755 (2006.01) C12N 9/64 (2006.01) C12N 9/74 (2006.01) C12N 15/82 (2006.01) A61K 38/00 (2006.01)

Patent

CA 2328493

A composition is provided for transgenic plants and transgenic plant derived human coagulation factors capable of eliciting an activation response in human blood clotting pathways and therefore useful for the treatment of human beings diagnosed to be deficient in blood clotting factor proteins. Such proteins may be manufactured by methods resulting in viral free production using both whole plants and plant cell cultures. Also provided are expression vectors for the proper transformation of plant tissue for the production of such factors, as well as transformed plant cells and processes for producing human coagulation factors using plant molecular biology techniques.

L'invention concerne une composition pour plantes transgéniques et pour des facteurs de coagulation humains dérivés de ces plantes transgéniques et capables d'éliciter une réaction d'activation dans le processus de coagulation et par conséquent utiles pour le traitement de patients humains chez lesquels une déficience des protéines du facteur de coagulation a été diagnostiquée. Ces protéines peuvent être produites par des procédés permettant une production non virale, comprenant l'utilisation de plantes entières et de cultures de cellules de plantes. L'invention concerne également des vecteurs d'expression assurant une transformation correcte du tissu végétal pour la production de ces facteurs, ainsi que des cellules de plantes transformées et des procédés permettant de produire des facteurs de coagulation humains par des techniques de biologie moléculaire végétale.

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