I-crei meganuclease variants with modified specificity,...

C - Chemistry – Metallurgy – 12 – N

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C12N 9/22 (2006.01) C12N 15/10 (2006.01) C12N 15/55 (2006.01) C12N 15/64 (2006.01) C12N 15/79 (2006.01) C12N 15/90 (2006.01)

Patent

CA 2600033

Method of preparing 1-CreI meganuclease variants having a modified cleavage specificity, variants obtainable by said method and their applications either for cleaving new DNA target or for genetic engineering and genome engineering for non-therapeutic purposes. Nucleic acids encoding said variants, expression cassettes comprising said nucleic acids, vectors comprising said expression cassettes, cells or organisms, plants or animals except humans, transformed by said vectors.

L'invention concerne un procédé de préparation de variantes de méganucléases I-CreI qui présentent une spécificité de clivage modifiée, des variantes pouvant être obtenues à l'aide de ce procédé, ainsi que leurs applications soit dans le clivage d'une nouvelle cible d'ADN soit dans le domaine du génie génétique et de la génomique à des fins non thérapeutiques. Par ailleurs, l'invention concerne des acides nucléiques codant ces variantes, des cassettes d'expression comprenant ces acides nucléiques, des vecteurs comprenant lesdites cassettes d'expression, ainsi que des cellules ou des organismes, des plantes ou des animaux, l'homme excepté, transformés par ces vecteurs.

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